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Работы, на которые ссылается эта работа

Работ: 335

Работа: CRISPR-Cas9-Based Technology and Its Relevance to Gene Editing in Parkinson’s Disease

  1. A Programmable Dual-RNA–Guided DNA Endonuclease in Adaptive Bacterial Immunity

    Martin Jínek, Krzysztof Chylinski, Ines Fonfara +3

    Статья2012Цитирований: 7
    ABI
  2. Multiplex Genome Engineering Using CRISPR/Cas Systems

    Le Cong, F. Ann Ran, David Cox +8

    Статья2013Цитирований: 4
    ABI
  3. CRISPR Provides Acquired Resistance Against Viruses in Prokaryotes

    Rodolphe Barrangou, Christophe Fremaux, Hélène Deveau +5

    Статья2007Цитирований: 4
    ABI
  4. Evolutionary classification of CRISPR–Cas systems: a burst of class 2 and derived variants

    Kira S. Makarova, Yuri I. Wolf, Jaime Iranzo +23

    Обзорная статья2019Цитирований: 4
    ABI
  5. Parkinson's disease

    Bastiaan R. Bloem, Michael S. Okun, Christine Klein

    Обзорная статья2021Цитирований: 4
    ABI
  6. Incidence of Parkinson's Disease: Variation by Age, Gender, and Race/Ethnicity

    Stephen K. Van Den Eeden

    Статья2003Цитирований: 3
    ABI
  7. 53BP1, BRCA1, and the Choice between Recombination and End Joining at DNA Double-Strand Breaks

    James M. Daley, Patrick Sung

    Обзорная статья2014Цитирований: 3
    ABI
  8. Repurposing CRISPR as an RNA-Guided Platform for Sequence-Specific Control of Gene Expression

    Lei S. Qi, Matthew H. Larson, Luke A. Gilbert +4

    Статья2013Цитирований: 3
    ABI
  9. Delivering CRISPR: a review of the challenges and approaches

    Christopher A. Lino, Jason C. Harper, James P. Carney +1

    Обзорная статья2018Цитирований: 3
    ABI
  10. DNA targeting specificity of RNA-guided Cas9 nucleases

    Patrick D. Hsu, David A. Scott, Joshua A. Weinstein +11

    Статья2013Цитирований: 2
    ABI
  11. CRISPR RNA maturation by trans-encoded small RNA and host factor RNase III

    Elitza Deltcheva, Krzysztof Chylinski, Cynthia M. Sharma +6

    Статья2011Цитирований: 2
    ABI
  12. Measuring and Reducing Off-Target Activities of Programmable Nucleases Including CRISPR-Cas9

    Taeyoung Koo, Jungjoon Lee, Jin‐Soo Kim

    Обзорная статья2015Цитирований: 2
    ABI
  13. Genome engineering using the CRISPR-Cas9 system

    F. Ann Ran, Patrick D. Hsu, Jason Wright +3

    Статья2013Цитирований: 2
    ABI
  14. RNA-Guided Human Genome Engineering via Cas9

    Prashant Mali, Luhan Yang, Kevin M. Esvelt +5

    Статья2013Цитирований: 2
    ABI
  15. High-frequency off-target mutagenesis induced by CRISPR-Cas nucleases in human cells

    Yanfang Fu, Jennifer A Foden, Cyd Khayter +4

    Статья2013Цитирований: 2
    ABI
  16. The blood-brain barrier: Bottleneck in brain drug development

    William M. Pardridge

    Обзорная статья2004Цитирований: 2
    ABI
  17. Viral vectors: a look back and ahead on gene transfer technology.

    Laura Vannucci, Michele Lai, Flavia Chiuppesi +2

    Статья2013Цитирований: 2
    ABI
  18. Parkinson's disease: clinical features and diagnosis

    Joseph Jankovic

    Обзорная статья2008Цитирований: 2
    ABI